Hereditary

Only one copy of a mutated gene is needed for the trait to manifest. Examples include Huntington’s disease and Marfan syndrome. If a parent has the mutation, each child has a 50% chance of inheriting it.

These genes are located on the X chromosome. Because males have only one X chromosome (XY), they are more likely to express X-linked hereditary disorders like hemophilia and Duchenne muscular dystrophy. Females (XX) are usually carriers. Hereditary

The goal is to move from managing diseases to curing them. Instead of treating a child with a hereditary immune deficiency, doctors want to edit the hematopoietic stem cells to correct the mutation permanently. While germline editing (changing eggs, sperm, or embryos) remains controversial due to ethical concerns, it represents the ultimate frontier: allowing parents to eliminate hereditary diseases from their bloodline forever. Only one copy of a mutated gene is